Federico Bolognani, M.D., Ph.D. Vice President, Head of Clinical Science, Axial Therapeutics Stuart Cobb, Ph.D. Chief Scientific Officer, Neurogene; Research Fellow, University of Edinburgh Yael Weiss, M.D., Ph.D. Vice President, Business Development, Ultragenyx Randy Carpenter, M.D. Chief Medical Officer, Rett Syndrome Research Trust; Co-Founder, Allos Pharma