Tag: Gene therapy

May 09, 2022

Gene therapies for GRIN disorder

March 16, 2022

Targeted restoration of chromatin regulators as therapeutic interventions for autism

January 01, 2021

Development of antisense oligonucleotides for SYNGAP1 haploinsufficiency associated with autism spectrum disorder and intellectual disability

January 01, 2021

Leveraging systemic adeno-associated viral vectors to ameliorate autism-associated phenotypes in a mouse model of neurofibromatosis type 1

September 01, 2020

Development of genetic therapies for STXBP1 haploinsufficiency

August 03, 2020

Antisense gene therapy for dominant haploinsufficiencies associated with autism